SMA is a genetic condition that impacts motor neurons, leading to muscle weakness that affects essential functions like breathing and movement. Treatments like Spinraza and Zolgensma can help manage ...

Spinal muscular atrophy (SMA) is a genetic neuromuscular condition caused by mutations in the SMN1 gene. SMA is characterized by symmetrical progressive (proximal predominant) muscle atrophy caused by ...

Reliable data on the costs of spinal muscular atrophy (SMA) illness are scarce, leaving key questions unanswered as new, high-priced therapies continue to emerge. Reliable data on the costs of spinal ...

SMA, which can affect up to 10,000 children around the world, comes under four main types: Types 1, 2 and 3 appear in childhood; Type 4, also known as adult-onset SMA, appears in adulthood. SMA Type 1 ...

Authors of a systematic literature review concluded more research is needed to better understand the financial burden of spinal muscular atrophy (SMA). More robust, long-term studies are needed to ...